Autologous HSPC-targeted LV Gene Therapy for Fanconi Anemia & LAD-I: An Update From Rocket Pharmaceuticals
Time: 9:00 am
day: Day One
Details:
- Specific challenges for cell- and gene-based therapy in life-threatening hematopoietic disorders.
- Fanconi anemia gene therapy program: updated results
- Leukocyte adhesion deficiency gene therapy program: updated results
