Gaining Insights into a Successful Hemophilia Gene Therapy Trial

Time: 10:00 am
day: Day Two

Details:

  • Overview standard outcomes measures and recent surrogate endpoints, safety measures, and patient important outcomes (PIOs) and patient reported outcomes (PROs)
  • Understand logistical considerations for early trial clinical development and scalable clinical product management
  • Examine patient selection and retention in hemophilia advanced therapy trials

Speakers: