Speakers

Allison Intondi

Senior Director, Head of Clinical Operations

Graphite Bio

Angela Johnson

Senior Director, Regulatory Affairs

Sigilon Therapeutics

John Pasi

Professor, Haemostasis & Thrombosis; Barts & the London School of Medicine

Principal Investigator, BioMarin Valoctocogene Roxaparvovec Program

Beverley Francis-Gibson

President & Chief Executive Officer

Sickle Cell Disease Association of America

Chris Takimoto

Senior Vice President

Gilead Sciences

Gabriela Denning

Vice President, Research & Development

Expression Therapeutics

Clark Paramore

Head of Value Demonstration, Vice President HEOR

bluebird bio

David Page

National Director of Health Policy

Canadian Hemophilia Society

Ian Winburn

Vice President, Global Medical Lead, Hemophilia, Endocrine & IEM, Rare Diseases

Pfizer

Alexandria Petrusich

Head of Translational Medicine

Graphite Bio

Julian Down

Senior Director, Gene Therapy

Poseida Therapeutics

Kate Zhang

Vice President

Editas Medicine

Lesha Shah

Assistant Professor, Medical Director, Child, Adolescent & Family Services, Icahn School of Medicine at Mount Sinai

Mount Sinai Health System

Mark Trusheim

Strategic Director, NEWDIGS & Visiting Scientist

MIT Sloan

Marcus Droege

Vice President & Head Global RWE

bluebird bio

Pablo Rendo

Global Project Head, Red Blood Disorders & Rare Disease Gene Therapy

Sanofi

Nick Li

Senior Director, Health Economics & Outcomes Research

UniQure

Nicolas Garnier

Director, Patient Advocacy

Pfizer

Paul Monahan

Clinical Development Lead, Hematology

Spark Therapeutics

Richard McFarland

President

Standards Coordinating Body (SCB)

Sandeep Soni

Executive Director, Clinical Development

CRISPR Therapeutics, Inc.

Matthew Birmingham

Senior Director, Supply Chain

bluebird bio

Steven Arkin

Executive Director, Clinical Research, Rare Diseases Research Unit, Pfizer Worldwide R&D

Pfizer

Wendy Pang

Executive Director, Research & Clinical Development

Jasper Therapeutics

Alexandra Hicks

Head of Dupixent Research, Immunology & Inflammation Research Therapeutic Area

Sanofi