Speakers




Beverley Francis-Gibson
President & Chief Executive Officer
Sickle Cell Disease Association of America








Lesha Shah
Assistant Professor, Medical Director, Child, Adolescent & Family Services, Icahn School of Medicine at Mount Sinai
Mount Sinai Health System

John Pasi
Professor, Haemostasis & Thrombosis; Barts & the London School of Medicine
Principal Investigator, BioMarin Valoctocogene Roxaparvovec Program









Steven Arkin
Executive Director, Clinical Research, Rare Diseases Research Unit, Pfizer Worldwide R&D
Pfizer


Alexandra Hicks
Head of Dupixent Research, Immunology & Inflammation Research Therapeutic Area
Sanofi


Alexandra Hicks
Head of Dupixent Research, Immunology & Inflammation Research Therapeutic Area
Sanofi